Pipeline analysis: 10x growth, but serious questions
Updated projection of US durable cell and gene therapies product-indication approvals based on December 2019 development pipeline. Ongoing pipeline modeling by the MIT NEWDIGS FoCUS team projects 10X growth from July 2020 levels, but with large uncertainties.
Paying for Cures Virtual Conference
This one-day virtual conference will share research and solutions to the challenge of paying for high cost, durable and curative therapies. Attendees will leave understanding the estimated clinical trial pipeline of these types of therapies and their potential impact on the healthcare system.
Paying for Cures Toolkit updated with new material for patients and developers
Version 2 of the free online resource adds new sections for patients and developers, and provides new downloadable references, in addition to the interactive analysis and calculation tools. Open the Toolkit
IN THE COMMUNITY
On behalf of the NEWDIGS initiative / FoCUS Project, project team members submitted comments on the recent CMS Proposed Rule supporting Value-Based Purchasing (VBP) (CMS-2482-P). With active input from an engaged set of our cross-sectoral members, we focused on the Proposed Rule as an important step forward in enabling outcomes-based contracting by addressing several Medicaid Best Price methodology challenges. We encouraged further efforts to promote use of the full range of precision financing solutions by addressing additional barriers for payment over time and subscription approaches. In addition, we suggested a number of areas where additional regulatory clarification or innovation would be helpful in regards to the approaches suggested in the Proposed Rule. Download the NEWDIGS comment (PDF)
On July 13 Mark Trusheim participated in a webinar hosted by the Institute for Gene Therapies entitled “CMS Proposed Rule on Value-based Purchasing”. Watch the recording
Jane Barlow will be speaking at Product Launch for Cell and Gene Therapies conference September 23–24 in Boston; the Annual Alpha Stem Cell Clinic Symposium October 7–8 in Sacramento; and the NAMCP Value Based Care Council presentation October 9 in Las Vegas.
The next FoCUS Design Lab will be held online October 15-16. By invitation only.